Gene Therapy, Bluebird
Worries Mount Over Cancer Risks in Bluebird Bio's Gene Therapy
Newly released data reveals that seven out of 67 children treated with Bluebird Bio Inc's (NASDAQ:BLUE) gene therapy for a severe neurological disorder in clinical trials have developed blood cancers.
7 children developed blood cancer after Bluebird Bio gene therapy for rare neurological disease
A Bluebird Bio gene therapy has helped children with a devastating neurological disorder, but seven have developed blood cancer, creating difficult choices for the families.
Gene Therapy for Rare Brain Disease Effective, but Comes With Blood Cancer Risk
While the use of elivaldogene autotemcel (eli-cel; Skysona) gene therapy has demonstrated long-term efficacy in patients with cerebral adrenoleukodystrophy (CALD), that benefit comes with a risk of developing hematologic cancers, according to results from a pair of studies.
7 children given bluebird's Skysona developed blood cancer: study
Seven out of 67 children who were given bluebird bio’s (NASDAQ:BLUE) gene therapy Skysona during clinical trials ended up developing blood cancer, according to a new study. Six of the children who received the treatment,
Bluebird bio’s Skysona led to seven cases of blood cancer in gene therapy trials
Whilst the events do not outline any new safety risks, the data gives a new understanding of the link between oncogenesis and Skysona.
Report gives update on boys with rare brain disease 6 years after gene therapy
Most boys treated with breakthrough gene therapy for a rare but deadly brain illness are faring well six years later, two new ...
STAT22h
Sarepta’s gene therapy is fully approved, but its stock has tanked. Here’s why
Since the FDA cleared Sarepta Thereapeutics' gene therapy for nearly all people with Duchenne, its stock price has tanked.
technologynetworks5h
Gene Therapy Enables Precise Magnetic Field Control of Brain Circuits
A new gene therapy technology enables the non-invasive control of specific brain circuits, holding promise for studying the ...
Gene therapy shows long-term benefit for patients with a rare pediatric brain disease
Cerebral adrenoleukodystrophy (CALD) is a rare, progressive, genetic brain disease that primarily presents in young boys, ...
Johns Hopkins Newsletter2d
Current progress and innovation for gene therapy delivery systems
As of October 2024, there are more than thirty FDA-approved gene therapies, spanning a diverse array of diseases such as ...
BioSpace2d
Cell and Gene Therapy Investment Ticks Up After Hard Few Years
Tim Hunt, CEO of the Alliance for Regenerative Medicine, said Monday at the 2024 Cell & Gene Meeting on the Mesa that ...
Topic: gene therapy
Despite a bumpy history, through work and trust, gene therapy may have a future. Treatments involve adding a new gene, or ...
News Medical on MSN1d
Novel gene therapy holds potential in treating patients with epilepsy
Researchers from the Yong Loo Lin School of Medicine, National University of Singapore (NUS Medicine) are working on a therapy that holds potential in treating patients with epilepsy, a neurological ...
BioSpace1d
Big Pharma’s Interest Grows in Evolving Cell and Gene Therapy Sector
Large pharmaceutical companies were out in force at this week’s 2024 Cell & Gene Meeting on the Mesa, as they look to expand ...
Gene Therapy Researcher's Patent Dispute Cleared to Proceed Against UPenn, Program Director
The court determined it wasn't required to dismiss the case pursuant to the defendants' statute of limitations argument, as ...