News

UConn, Connecticut Children’s conducting world’s first gene-editing trial for rare disease: ‘fixing it at its source’
It is trying to treat a devastating lifelong disease by fixing it at its source. We are able to fix the actual genetic ...
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Cystic Fibrosis Foundation Commits Up to an Additional $24 Million for Prime Medicine to Develop Gene Editing Therapy
BETHESDA, Md. (July 16, 2025) – Today, the Cystic Fibrosis Foundation announced an additional investment of up to $24 million ...
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FDA questions safety of GSK’s multiple myeloma drug
From my colleague Drew Joseph: Ahead of an advisory committee meeting Thursday focused on GSK’s multiple myeloma drug Blenrep, the FDA pointed to concerns about the high rates of eye issues that have ...