Gene therapy for hereditary spastic paraplegia hits proof-of-principle milestone

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University's College ...

Common medicines may influence CRISPR therapy outcomes and precision cancer treatment

In a new study, scientists at the Max Planck Institute for Evolutionary Anthropology in Leipzig analyzed the impact of more ...
Healio

STUDY: Voretigene neparvovec offers sustained light sensitivity improvement

A 5-year interim analysis of the PERCEIVE real-world study showed sustained improvement of light sensitivity in patients ...
Drexel University

Breakthrough on Gene Therapy for Hereditary Spastic Paraplegia

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University’s College ...
STAT

Child’s sudden death unnerves a promising area of gene therapy research

Researchers hoped they had finally found a way to get gene therapies past the blood-brain barrier. Then the first patient ...