A mom was overjoyed when she learned a gene therapy treatment could save her child's life, until she found out no one would ...

A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a ...

To our immune system, a potentially lifesaving gene therapy can look a lot like a dangerous infection. That's because most ...

A once-beleaguered gene-therapy stock just landed a major vote of confidence—and the timing seems anything but accidental.

SAN DIEGO (KGTV) - The family of a 4-year-old girl given a grim diagnosis is giving thanks this holiday season amid some stunning signs in the past few weeks. A groundbreaking treatment taken on by ...

Copyright 2025 The Associated Press. All Rights Reserved. Copyright 2025 The Associated Press. All Rights Reserved. At The Gentle Barn, this flock of turkeys isn’t ...

Oliver Chu has shown “dramatic improvements” following the groundbreaking treatment, his father Ricky Chu said The University of Manchester (MFT) Oliver Chu, 3, was born with a rare genetic condition ...

Huntington’s disease is one of the cruelest genetic afflictions a family can endure. The condition, which affects around 41,000 Americans, is the result of an error ...

ALS Network and ALS United awarded 13 research grants aimed at enhancing ALS understanding and care. Projects focus on biomarkers, genetic causes (C9ORF72, TDP-43), environmental risks, and motor ...

London – 25 November 2025 - Purespring Therapeutics, a precision nephrology company leading the development of targeted, first-in-class genetic therapies to preserve kidney function, today announced ...

Purespring Therapeutics to Present at Piper Sandler’s 37th Annual Healthcare Conference London – 25 November 2025 - Purespring Therapeutics, a precision nephrology company leading the development of ...