A mom was overjoyed when she learned a drug could save her baby's life. Then she learned it cost $2 million.

A mom was overjoyed when she learned a gene therapy treatment could save her child's life, until she found out no one would ...

Breakthrough genetic therapies can save lives, but many cost millions for single dose

A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a ...

Circular single-stranded DNA molecules for safer genetic medicine

To our immune system, a potentially lifesaving gene therapy can look a lot like a dangerous infection. That's because most ...

Precigen Stock Up 280% in a Year — Is FDA Approval Behind This Big New Investor Bet?

A once-beleaguered gene-therapy stock just landed a major vote of confidence—and the timing seems anything but accidental.
People

3-Year-Old Boy with Rare Condition Amazes Doctors by Becoming World's First Gene Therapy Patient

Oliver Chu has shown “dramatic improvements” following the groundbreaking treatment, his father Ricky Chu said The University of Manchester (MFT) Oliver Chu, 3, was born with a rare genetic condition ...
The Washington Post

Thankful for breakthroughs in gene therapy

Huntington’s disease is one of the cruelest genetic afflictions a family can endure. The condition, which affects around 41,000 Americans, is the result of an error ...
KXAN

Peer-Reviewed: MarinBio’s Novel Cell-Based Potency Assay for Gene Therapy

MarinBio publishes validated GMP/GLP cell-based potency assay for AAV-delivered anti-CD3-anti-CD19 diabody (GP101) in Journal of Immunological Methods. This publication is a milestone for the cell & ...
The Business Journals

'The future of medicine': Cincinnati Children's dedicates new $60M center in Sharonville

Cincinnati Children's is nearly ready to move into its new Applied Gene and Cell Therapy Center in Sharonville, a $60 million project. DAVID STEPHEN FOR ACBJ To ...