Learn how to navigate cystic fibrosis care with confidence, from treatments and school plans to building a supportive medical ...

ReCode Therapeutics, a clinical-stage genetic medicines company using tissue-specific delivery to power the next wave of mRNA ...

Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...

The Adeno Associated Virus Vector Manufacturing market, valued at USD 1,148.4 million in 2024, is expected to register robust revenue CAGR of 19.6%.Request free copy of this report:  March 14, 2025 - ...

The Cystic Fibrosis Foundation will host Acadiana’s Finest, a campaign to raise funds and awareness for cystic fibrosis and recognize the area’s top young professional leaders.

Learning from examples like congenital heart disease and cystic fibrosis can help health systems and clinicians prepare to care for an influx of patients with neuromuscular diseases as they reach ...

Cystic fibrosis (CF) patients could be given access to a new drug on the NHS by the end of the year if it is given the green ...

The genetic condition cystic fibrosis had no treatments on the NHS before 2019 and a Daily Express campaign - now a miracle ...

A new research project focusing on rare genetic mutations that are linked to cystic fibrosis just received $600,000 in ...

The biotech won approval for its first cystic fibrosis (CF) drug -- Kalydeco -- back in 2012 ... collecting approvals for a gene-editing therapy for blood disorders a little over a year ago and a pain ...

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“This is the beginning of a new era of medicine,” said Dr. Kiran Musunuru, a gene therapy researcher at the University of Pennsylvania’s Perelman School of Medicine. He added that the method ...