But her career arc slowly bent back toward that childhood revelation. Today, Stueland is the CEO of GeneDx, a publicly traded ...

Learn how to navigate cystic fibrosis care with confidence, from treatments and school plans to building a supportive medical ...

Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...

The Cystic Fibrosis Foundation will host Acadiana’s Finest, a campaign to raise funds and awareness for cystic fibrosis and recognize the area’s top young professional leaders.

Cystic fibrosis (CF) patients could be given access to a new drug on the NHS by the end of the year if it is given the green light by the service’s spending watching. The National Institute for Health ...

The genetic condition cystic fibrosis had no treatments on the NHS before 2019 and a Daily Express campaign - now a miracle one-a-day pill could make it vanish.

Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders. Now it’s on the cusp of its first regulatory approval. Each year ...

Cystic fibrosis (CF) is a genetic condition that affects the lungs, pancreas and other organs, caused by variations on the cystic fibrosis transmembrane conductance regulator?(CFTR) gene.

The biotech won approval for its first cystic fibrosis (CF) drug -- Kalydeco -- back in 2012 ... collecting approvals for a gene-editing therapy for blood disorders a little over a year ago and a pain ...

Vertex Pharmaceuticals’ triple combination cystic fibrosis (CF) treatment has been approved ... by correcting the malfunctioning protein made by the CFTR gene. The MHRA’s approval of the therapy was ...