Adeno-associated virus (AAV)–mediated gene therapy was one of the focal points of this year's Muscular Dystrophy Association conference. Here, Barry Byrne, MD, PhD, University of Florida, speaks to ...
Tel Aviv University scientists say that they can inject CRISPR genetic 'molecular scissors' to shrink tumors by 90%; ...
Stem cell therapy has emerged as a groundbreaking treatment option for corneal injuries, offering hope to individuals ...
The American Association for Cancer Research (AACR) today announced its newly elected 2025 class of Fellows of the AACR Academy.
Elsewhere in gene-based eye care, MeiraGTx is advancing its investigational gene therapy toward expedited approval in the UK after 11 children who were born blind from birth gained significant vision ...
UNC Charlotte researchers are contributing to pioneering breakthroughs in cancer therapeutics, communicable disease ...
Four young children with a rare inherited eye disorder gained meaningful sight after a single gene therapy treatment . The children went from only being able to tell light from darkness to being ...
The others segment is expected to grow at a significant CAGR over the forecast period. Gene therapy is a medical field in which disease is prevented and cured by replacing an underlying genetic ...
Ten of 11 children born profoundly deaf experienced some degree of hearing improvement after receiving an experimental gene therapy developed by Regeneron Pharmaceuticals. A few of the children can ...
Regeneron’s investigational gene therapy has been tied to notable hearing improvements in 10 of 11 children who were treated for a rare genetic condition that causes hearing loss. “You can see ...