Most patients with a rare and aggressive form of large B-cell lymphoma can safely receive a less toxic treatment than the ...

This year, gene-editing technology was customized to fix mutations in a single patient’s genes for the first time.

When weird fungal epidemics crop up in far-flung places, scientists work together to unravel how the microscopic murderers ...

H5N1 bird flu has been circulating in U.S. wildlife since late 2021 but has caused only one human fatality. Now a different ...

Think your seasonal allergies are bad? Some people are allergic to water, cold temperatures, or even exercise. Explore the science behind the world's rarest allergies.

Across America, millions of parents of children with rare diseases are in a race against time, hoping that new treatments will be developed fast enough to save their kids. Thanks to advances in ...

US regulators laid out new guidelines for approving custom-made treatments for individual patients, a move that could bring the promise of gene editing to more people with devastating diseases. Food ...

NEW YORK, Nov 12 (Reuters) - The U.S. Food and Drug Administration can approve new personalized treatments for rare and deadly genetic diseases based on data from a handful of patients, two of the ...

The authors do not work for, consult, own shares in or receive funding from any company or organization that would benefit from this article, and have disclosed no relevant affiliations beyond their ...

Charlie Evans, 13, who suffers from severe food allergies and eosinophilic esophagitis (EoE), takes part in an NIH-funded study at Cincinnati Children's hospital. The NIH dismissed the hospital's ...