Most boys treated with breakthrough gene therapy for a rare but deadly brain illness are faring well six years later, two new ...

Most boys treated with breakthrough gene therapy for a rare but deadly brain illness are faring well six years later, two new ...

A new technology enables the control of specific brain circuits non-invasively with magnetic fields, according to a ...

Since the FDA cleared Sarepta Thereapeutics' gene therapy for nearly all people with Duchenne, its stock price has tanked.

Pfizer shared that the combination of its drugs Talzenna and Xtandi extended survival in men with metastatic ...

Seven out of 67 children who were given bluebird's (BLUE) gene therapy Skysona during clinical trials ended up developing ...

Researchers have developed a breakthrough technology using magnetic fields to control specific brain circuits non-invasively, ...

Immunotherapy, using a patient's own immune system to treat disease, has shown promise in some patients with cancer but has ...

LCA16 is a retinal dystrophy resulting from a genetic mutation which expresses a critical ion channel in retinal pigment epithelium cells.

Hematologic cancer develops in some patients receiving lentiviral elivaldogene autotemcel (eli-cel) gene therapy for cerebral ...

A newly developed soft robotic finger with a sophisticated sense of touch could one day help your doctor perform routine ...

A new technology enables the control of specific brain circuits non-invasively with magnetic fields, according to a preclinical study from researchers at Weill Cornell Medicine, The Rockefeller ...