Most boys treated with breakthrough gene therapy for a rare but deadly brain illness are faring well six years later, two new ...

While the use of elivaldogene autotemcel (eli-cel; Skysona) gene therapy has demonstrated long-term efficacy in patients with ...

Newly released data reveals that seven out of 67 children treated with Bluebird Bio Inc's (NASDAQ:BLUE) gene therapy for a ...

A new technology enables the control of specific brain circuits non-invasively with magnetic fields, according to a ...

Researchers from the Yong Loo Lin School of Medicine, National University of Singapore (NUS Medicine) are working on a ...

Since the FDA cleared Sarepta Thereapeutics' gene therapy for nearly all people with Duchenne, its stock price has tanked.

A Bluebird Bio gene therapy has helped children with a devastating neurological disorder, but seven have developed blood ...

Cerebral adrenoleukodystrophy (CALD) is a rare progressive, genetic brain disease that primarily presents in young boys, ...

London-based biotech Purespring Therapeutics plans to bring their kidney-tweaking gene therapy to the clinic with the help of ...

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Despite a bumpy history, through work and trust, gene therapy may have a future. Treatments involve adding a new gene, or ...