A Bluebird Bio gene therapy has helped children with a devastating neurological disorder, but seven have developed blood ...

Researchers will develop therapies for urea cycle disorders and create a platform to rapidly develop treatments for other rare genetic disorders.

A new technology enables the control of specific brain circuits non-invasively with magnetic fields, according to a ...

A new gene drive can copy and paste itself into the genomes of herpes simplex viruses in mice. The end goal is a version that disables the virus in humans.

Since the FDA cleared Sarepta Thereapeutics' gene therapy for nearly all people with Duchenne, its stock price has tanked.

Most boys treated with breakthrough gene therapy for a rare but deadly brain illness are faring well six years later, two new ...

Purespring raises £80 million in a Series B financing, with Syncona committing £19.9 million[1] as part of a leading syndicate of life science investorsProceeds will be used to advance Purespring’s ...

Our round-up of recent biotech financings features a strong first round for City Therapeutics, a new RNAi venture led by ...

Purespring Therapeutics Ltd. has raised £80 million (US$104.6 million) in a series B, putting it on course to be the first to ...

Biotechnology company Purespring Therapeutics has raised about $105 million to fund its development of gene therapies for ...

Purespring Therapeutics, a UK-based gene therapy company focused on kidney disease, has raised £80 million ($105 million) in ...

The London-based firm said it will use the funds to advance its gene therapy pipeline, including its lead program in IgA nephropathy.