It is trying to treat a devastating lifelong disease by fixing it at its source. We are able to fix the actual genetic ...

BETHESDA, Md. (July 16, 2025) – Today, the Cystic Fibrosis Foundation announced an additional investment of up to $24 million ...

While the CRL derails a near-term clearance, one analyst described the rejection as more of “a speed bump to approval, rather ...

The firm said the agency cited chemistry, manufacturing, and controls issues in its complete response letter, but had no concerns about product quality.

In his first 100 days as commissioner of the Food and Drug Administration, Marty Makary has made a handful of splashy ...

As predicted the era of universal newborn genomic screening is dawning. The UK and Florida are leading the way.

CRISPR Therapeutics is revolutionizing medicine with gene editing. Learn more about CRSP's breakthroughs, stock rally, and ...

A team of researchers from the University of Maryland School of Medicine (UMSOM) recently won a $250,000 prize from the ...